A rare focus on patients and their families.

Rare diseases affect 30 million people in the United States (1 in 10 Americans) and their families and 350 million people globally. Further, 50 percent of these rare diseases affect children, making rare diseases among the most deadly and debilitating disease categories affecting our kids. According to estimates, 95 percent of all rare diseases do not have a single FDA approved drug treatment.

Our goal is to develop and commercialize important and novel products for patients and their families suffering from certain rare and near-rare neuropsychiatric conditions.